Noninvasive gene delivery to foveal cones for vision restoration
Khabou, Hanen, Garita-Hernandez, Marcela, Chaffiol, Antoine, Reichman, Sacha, Jaillard, Céline, Brazhnikova, Elena, Bertin, Stéphane, Forster, Valérie, Desrosiers, Mélissa, Winckler, Céline, Goureau, Olivier, Picaud, Serge, Duebel, Jens, Sahel, José-Alain, Dalkara, Deniz·2018·JCI Insight
Cited by (124)
Items 101–124 of 124
- Combined Expression of hRdCVF and hRdCVFL Through AAV-Mediated Delivery for the Treatment of Retinitis PigmentosaEmmanuelle Clérin, Ying Yang, Delphine Pagan, Seiki Achiedo, Frédéric Blond, Géraldine Millet-Puel, Najate Aït-Ali, Imen Harichane, Julie Dégardin, Quénol Cesar et al. · 2026 · Investigative Ophthalmology & Visual Science
- Optogenetics for therapeutic use in the brain, eye, and earBenjamin Ng, Robert Edward MacLaren, Jasmina Cehajic‐Kapetanovic · 2026 · Handbook of clinical neurology
- Adeno-associated Viral Vectors in the Retina: Delivering Gene Therapy to the Right DestinationNoam D. Rudnick, Leo A. Kim, Jason Comander · 2022 · International Ophthalmology Clinics
- Disease exacerbation by fibroblast inclusion in Duchenne Muscular Dystrophy MYOrganoids reveals limitations of microdystrophin therapeutic efficacyLaura Palmieri, Louna Pili, Abbass Jaber, Ai Vu Hong, Matteo Marcello, Riyad El‐Khoury, Guy Brochier, Anne Bigot, David Israeli, Isabelle Richard et al. · 2023 · bioRxiv (Cold Spring Harbor Laboratory)
- Gene therapy in animal modelsClaudio Punzo · 2019 · Elsevier eBooks
- Moodle:データベース構築の実際(2)「小テスト」と「オンラインテキスト」について正幸 表 · 2010
- Morphology study in block copolymer electrolytesScott A. Mullin, Nisita S. Wanakule, Nitash P. Balsara · 2008 · Bulletin of the American Physical Society
- Faculty Opinions recommendation of Restoration of visual function by transplantation of optogenetically engineered photoreceptors.Gordon Fain · 2019 · Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
- Optogenetic Prosthetization of Retinal Bipolar CellsA. Yu. Rotov, M. L. Firsov · 2022 · Journal of Evolutionary Biochemistry and Physiology
- Investigation of the maximum feasible volume of subretinal injections into rat and cynomolgus monkey eyesMegumi Sakata, Tomoaki Araki, Masayuki Tomohiro · 2023 · Fundamental Toxicological Sciences
- Dopamine tracks adaptive learning of action representationsMaxime Côme, Arnaud Lespart, Aylin Gulmez, Loussineh Keshishian, Joachim Jehl, Elise Bousseyrol, Steve Didienne, Éléonore Vicq, Tinaïg Le Borgne, Alexandre Mourot et al. · 2024 · bioRxiv (Cold Spring Harbor Laboratory)
- The Role of Thermal Stability in AAV Titration of Engineered VariantsEmilia A. Zin, Mélissa Desrosiers, Tommaso Ocari, Guillaume Labernède, Camille Robert, Charlotte Izabella, Bruno Saubaméa, Ulisse Ferrari, Deniz Dalkara · 2024 · bioRxiv (Cold Spring Harbor Laboratory)
- Disease exacerbation in MYOrganoids derived from Duchenne Muscular Dystrophy iPSC reveals limitations of microdystrophin therapeutic efficacySonia Albini, Laura Palmieri, Louna Pili, Abbass Jaber, Ai Vu Hong, Melissa Moula, Riyad El‐Khoury, Guy Brochier, Anne Bigot, David Israeli et al. · 2025 · Research Square
- Reactivating the phototransduction cascade with a mutation agnostic gene therapy preserves vision in rod-cone dystrophiesCardillia-Joe Simon, Hanen Khabou, Antoine Chaffiol, Marco Rucli, Marion Finzi, Nathaniel Norberg, Anaïs Grimaud, Brix Mücher, Mélissa Desrosiers, Serge Sancho et al. · 2025 · iScience
- Advances in viral and nonviral delivery systems for therapeutic gene editingWeiyan Jiang, Hyun Chul Jeong, Jeong Hun Kim · 2025 · Taiwan Journal of Ophthalmology
- Development of safe and efficient aav vectors for retinal gene therapyHanen Khabou · 2018 · theses.fr (ABES)
- Rôle des récepteurs nicotiniques des circuits de l'addiction à la nicotine : une manipulation originale des récepteurs grâce à la lumièreSarah Mondoloni · 2020 · theses.fr (ABES)
- A new gene therapy approach to restore light sensitivity in Rod-Cone DystrophiesCardillia-Joe Simon · 2019 · theses.fr (ABES)
- Diversité des effets de la nicotine sur les neurones dopaminergiques de l’aire tegmentale ventraleClaire Nguyen · 2020 · theses.fr (ABES)
- Better understanding of the ON-bipolar cell signaling cascade and development of therapies for congenital stationary night blindnessJuliette Varin · 2020 · theses.fr (ABES)
- Dynamiques dopaminergiques dans la prise de décision : rôle dans la variabilité et l’explorationMaxime Côme · 2023 · theses.fr (ABES)
- Generation and Characterization of Patient-Derived Human Pluripotent Stem Cell Lines for Retinal Gene TherapyNathan Ehrenreich, Thibaud Metais, Marcela Garita‐Hernandez · 2026 · Methods in molecular biology
- Vision restoration: From prostheses to genetic-based brain–machine interfacesIgnacio Alcala, ERWAN DESAILLY, Fabrice Arcizet, Katia Marazova, Grégory Gauvain, Serge A. Picaud · 2026 · Handbook of clinical neurology
- Advances in neural organoids: structural organization, disease modeling, and applications in gene therapyEvelina Nasybullina, Elvira Ruslanovna Akhmetzyanova, Albert Anatolyevich Rizvanov, Yana Olegovna Mukhamedshina · 2026 · Molecular Biology Reports