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Liver Gene Therapy: Reliable and Durable

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Parvovirus-Derived Endogenous Viral Elements in Two South American Rodent Genomes

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AAV6 Is Superior to Clade F AAVs in Stimulating Homologous Recombination-Based Genome Editing in Human HSPCs

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An endogenous adeno-associated virus element in elephants

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In Vivo Delivery of Cassettes Encoding Anti-HBV Primary MicroRNAs Using an Ancestral Adeno-Associated Viral Vector

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A directed evolution approach to select for novel Adeno-associated virus capsids on an HIV-1 producer T cell line

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A DYSENTERY-LIKE BACILLUS FROM A PHLEGMONOUS INFLAMMATION

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Spatial Transcriptomics: Technical Aspects of Recent Developments and Their Applications in Neuroscience and Cancer Research

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Designing and optimizing AAV-mediated gene therapy for neurodegenerative diseases: from bench to bedside

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T-cell specific in vivo gene delivery with DART-AAVs targeted to CD8

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Strategies for Targeting Retroviral Integration for Safer Gene Therapy: Advances and Challenges

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Machine-learning-guided Directed Evolution for AAV Capsid Engineering

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The deLIVERed promises of gene therapy: Past, present, and future of liver-directed gene therapy

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AAV-mediated gene therapy for galactosialidosis: A long-term safety and efficacy study

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AAV2 and AAV9 tropism and transgene expression in the mouse eye and major tissues after intravitreal and subretinal delivery

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Adeno-Associated Viruses for Modeling Neurological Diseases in Animals: Achievements and Prospects

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Therapeutic Potential of Intrabodies for Cancer Immunotherapy: Current Status and Future Directions

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Serum factors create species-specific barriers to hepatic gene transfer by lipid nanoparticles in liver-humanized mice

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Delivery challenges for CRISPR—Cas9 genome editing for Duchenne muscular dystrophy

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Therapeutic Application and Structural Features of Adeno-Associated Virus Vector

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Current Advances in Adeno-Associated Virus-Mediated Gene Therapy to Prevent Acquired Hearing Loss

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Mucopolysaccharidosis type IIIB: a current review and exploration of the AAV therapy landscape

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AAV-mediated gene therapy for sialidosis

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Dissolving Microneedles for Nucleic Acid Delivery: A Systematic Search, Review, and Data Synthesis

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Tissue blood volumes and weights in adult beagle dogs.

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Liver-Humanized NSG-PiZ Mice Support the Study of Chronic Hepatitis B Virus Infection and Antiviral Therapies

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Control of HSV-1 Infection: Directions for the Development of CRISPR/Cas-Based Therapeutics and Diagnostics

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Development and evaluation of a mouse model susceptible to severe fever with thrombocytopenia syndrome virus by rAAV-based exogenous human DC-SIGN expression

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Inhibition of miR-25 ameliorates cardiac and skeletal muscle dysfunction in aged mdx/utrn haploinsufficient (+/−) mice

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Anticancer effect of the oncolytic Newcastle disease virus harboring the PTEN gene on glioblastoma

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Designer Organs: Ethical Genetic Modifications in the Era of Machine Perfusion

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rAAV-PHP.B escapes the mouse eye and causes lethality whereas rAAV9 can transduce aniridic corneal limbal stem cells without lethality

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Gene therapy for neurodegenerative disorders in children: dreams and realities

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Deep Mutational Scanning of the AAV rep Gene to Assess Effects on DNA Packaging in Expi293F Suspension Culture

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Adeno-associated Virus-Mediated Gene Delivery Across the Blood-Brain Barrier

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Recombinant adeno-associated viruses as a gene delivery vehicle for the use in molecular medicine

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Multi-step engineered adeno-associated virus enables whole-brain mRNA deliveryPreprint

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Viral vectors: design and delivery for small RNA

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Development and Validation of AAV-Mediated Liver, Liver-VAT, and Liver-Brain SORT and Therapeutic Regulation of FASN in Hepatic De Novo Lipogenesis

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Transgene Expression in Cultured Cells Using Unpurified Recombinant Adeno-Associated Viral Vectors

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A multiplexed barcode approach to simultaneously evaluate gene delivery by adeno-associated virus capsid variants in nonhuman primates

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Liver humanized NSG-PiZ mice support the study of chronic hepatitis B virus infection and antiviral therapiesPreprint

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Evaluation of Purification Methods for Minimizing Transgene Expression Background During Viral Manufacturing

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Viruses for Systemic Delivery

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JoVE Video Dataset

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Development of an Enzyme-Linked Immunosorbent Spot Assay for the Assessment of Adeno-Associated Virus Peptides to Examine Immune Safety

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Proof-of-Concept of a DNA-Based Recording System for High-Throughput Functional Gene Screening

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Site-Specific Capsid Modification Enables FRα-Directed Retargeting of AAV for Precision Gene Delivery

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Advancing the current state of gene therapies using adeno-associated virus vectors to treat atrial cardiomyopathy

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Initial efforts of translational development of AAV-encoded NaViPA1 for peripherally targeted analgesia in neuropathic pain

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Precision nanomedicine for antiviral therapeutics

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Reprogramming AAV tropism with tumor-associated targeting ligands

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Custom Adeno-Associated Virus Capsids: The Next Generation of Recombinant Vectors with Novel Tropism

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