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RNA-Targeting CRISPR/CasRx system relieves disease symptoms in Huntington’s disease models

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Human Bone Marrow-Derived Mesenchymal Stem Cell Applications in Neurodegenerative Disease Treatment and Integrated Omics Analysis for Successful Stem Cell Therapy

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Cell Reprogramming to Model Huntington’s Disease: A Comprehensive Review

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Patient-Specific iPSCs-Based Models of Neurodegenerative Diseases: Focus on Aberrant Calcium Signaling

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Early whole-body mutant huntingtin lowering averts changes in proteins and lipids important for synapse function and white matter maintenance in the LacQ140 mouse model

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The Big Picture of Neurodegeneration: A Meta Study to Extract the Essential Evidence on Neurodegenerative Diseases in a Network-Based Approach

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Discovery of new epigenomics-based biomarkers and the early diagnosis of neurodegenerative diseases

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Phenotyping Neurodegeneration in Human iPSCs

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Engineering Organoids for in vitro Modeling of Phenylketonuria

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Neural stem cells derived from the developing forebrain of YAC128 mice exhibit pathological features of Huntington’s disease

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CAG repeat expansions create splicing acceptor sites and produce aberrant repeat-containing RNAs

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Nicotinamide Adenine Dinucleotide Phosphate Oxidases Are Everywhere in Brain Disease, but Not in Huntington’s Disease?

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Triplet-Net Classification of Contiguous Stem Cell Microscopy Images

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Oligonucleotides Targeting DNA Repeats Downregulate Huntingtin Gene Expression in Huntington's Patient-Derived Neural Model System

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Systematic Evaluation of Extracellular Coating Matrix on the Differentiation of Human-Induced Pluripotent Stem Cells to Cortical Neurons

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Neuron-derived extracellular vesicles in plasma present a potential non-invasive biomarker for Huntingtin protein and RNA assessment in Huntington diseasePreprint

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The Evolution of Stem Cells, Disease Modeling, and Drug Discovery for Neurological Disorders

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A Progressive Loss of phosphoSer138-Profilin Aligns with Symptomatic Course in the R6/2 Mouse Model of Huntington’s Disease: Possible Sex-Dependent Signaling

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Synaptic and functional alterations in the development of mutant huntingtin expressing hiPSC‐derived neurons

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Transcriptomic Characterization Reveals Disrupted Medium Spiny Neuron Trajectories in Huntington’s Disease and Possible Therapeutic AvenuesPreprint

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A human CAGinSTEM platform for decoding HTT repeats’ somatic instability links CAG interruption to HD pathology in neurons

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Cerulenin partially corrects the disrupted developmental transcriptomic signature in Huntington’s disease striatal medium spiny neurons

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Distinct sub-cellular autophagy impairments occur independently of protein aggregation in induced neurons from patients with Huntington’s diseasePreprint

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Therapeutic validation of MMR-associated genetic modifiers in a human ex vivo model of Huntington’s diseasePreprint

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RNA Editing by ADAR Adenosine Deaminases in the Cell Models of CAG Repeat Expansion Diseases: Significant Effect of Differentiation from Stem Cells into Brain Organoids in the Absence of Substantial Influence of CAG Repeats on the Level of Editing

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Abnormal neurodevelopment predisposes to cortical hyperexcitability in Huntington's disease

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Iloperidone treatment mitigates the Juvenile Huntington's Disease phenotype possibly via Sigma‐1 Receptor Modulation

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Enhanced Differentiation of Human Neural Stem Cells into Cortical Neurons Using 3D Chitosan Scaffolds

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A potential role for NADPH oxidase (NOX1/2) in mutant huntingtin-induced anomalous neurite outgrowth

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Emerging Methods in Modeling Brain Development and Disease with Human Pluripotent Stem Cells

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Omics and Network-based Approaches in Understanding HD Pathogenesis

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Sodium channel Nav1.2-L1342P variant displaying complex biophysical properties renders hyperexcitability of cortical neurons derived from human iPSCsPreprint

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Stage-Specific Serum Proteomic Signatures Reveal Early Biomarkers and Molecular Pathways in Huntington’s Disease Progression

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Old enough to be a model? On the role of maturity in stem cell-based models for neuropsychiatric disorders

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A semi-automated MEA spike sorting method for high-throughput assessment of cultured neurons

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