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Infectious Clones and Vectors Derived from Adeno-Associated Virus (AAV) Serotypes Other Than AAV Type 2

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Cloning and Characterization of Adeno-Associated Virus Type 5

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Highly Purified Recombinant Adeno-Associated Virus Vectors Are Biologically Active and Free of Detectable Helper and Wild-Type Viruses

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Reversal of Blindness in Animal Models of Leber Congenital Amaurosis Using Optimized AAV2-mediated Gene Transfer

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Cell Lines for the Production of Recombinant Adeno-Associated Virus

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Quantification of adeno-associated virus particles and empty capsids by optical density measurement

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Adeno-Associated Virus Vectors in Clinical Trials

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Purification of Recombinant Adeno-Associated Virus Vectors by Column Chromatography and Its Performance in Vivo

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Scalable Purification of Adeno-Associated Virus Type 2, 4, or 5 Using Ion-Exchange Chromatography

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Identification of factors that contribute to recombinant AAV2 particle aggregation and methods to prevent its occurrence during vector purification and formulation

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Separation of adeno-associated virus type 2 empty particles from genome containing vectors by anion-exchange column chromatography

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Purification of recombinant adeno-associated virus type 8 vectors by ion exchange chromatography generates clinical grade vector stock

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The Cutter incident: how America's first polio vaccine led to the growing vaccine crisis

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Evidence for Encapsidation of Prokaryotic Sequences during Recombinant Adeno-Associated Virus Production and Their in Vivo Persistence after Vector Delivery

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Factors Affecting the Efficiency of CD8+ T Cell Cross-Priming with Exogenous Antigens

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A Versatile and Scalable Two-Step Ion-Exchange Chromatography Process for the Purification of Recombinant Adeno-associated Virus Serotypes-2 and -5

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Recombinant adeno-associated virus: formulation challenges and strategies for a gene therapy vector.

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Serum-free production and column purification of adeno-associated virus type 5

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Current status of gene therapy trials for Parkinson's disease

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Economized large‐scale production of high yield of rAAV for gene therapy applications exploiting baculovirus expression system

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Infectious Titer Assay for Adeno-Associated Virus Vectors with Sensitivity Sufficient to Detect Single Infectious Events

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GUIDANCE FOR INDUSTRY QUALITY SYSTEMS APPROACH TO PHARMACEUTICAL CGMP REGULATIONS

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The Cutter Incident: How America’s First Polio Vaccine Led to the Growing Vaccine Crisis

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900. Packaging of Host Cell and Plasmid DNA into Recombinant Adeno-Associated Virus Particles Produced by Triple Transfection

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1013. In Vivo Performance of AAV2 Vectors Purified by CsCl Gradient Centrifugation or Column Chromatography

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Lot Release and Characterization Testing of Live-Virus-Based Vaccines and Gene Therapy Products, Part 1 Factors Influencing Assay Choices

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Bioseparation: Proteins

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Quantifying Capsid Peptide:MHC I Complexes Following Adeno-Associated Virus (AAV) Transduction

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Trace Capsid DNA Impurities in AAV2 Vectors Are Not Transcribed and Are Unlikely To Contribute to Capsid Peptide-MHC Class I Complexes

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721. Intravenous Injection Cofactors of Adeno-Associated Virus Produce Varying Tissue-Specific Transduction Levels in Adult Mice

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Adeno-Associated Virus (AAV) as a Vector for Gene Therapy

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Emerging issues in AAV-mediated in vivo gene therapy

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Adeno-associated virus as a delivery vector for gene therapy of human diseases

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Human Immune Responses to Adeno-Associated Virus (AAV) Vectors

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Overcoming Preexisting Humoral Immunity to AAV Using Capsid Decoys

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Pharmacology of Recombinant Adeno-associated Virus Production

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Thermal Stability as a Determinant of AAV Serotype Identity

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AAV-PHP.B Administration Results in a Differential Pattern of CNS Biodistribution in Non-human Primates Compared with Mice

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Adeno-Associated Virus Gene Therapy for Liver Disease

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AAV vectors applied to the treatment of CNS disorders: Clinical status and challenges

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Choice of template delivery mitigates the genotoxic risk and adverse impact of editing in human hematopoietic stem cells

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Current challenges in biotherapeutic particles manufacturing

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Transient transfection methods for clinical adeno-associated viral vector production

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Comparison of analytical techniques to quantitate the capsid content of adeno-associated viral vectors

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Developing an Anion Exchange Chromatography Assay for Determining Empty and Full Capsid Contents in AAV6.2

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Emerging Technologies for Delivery of Biotherapeutics and Gene Therapy Across the Blood–Brain Barrier

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Adeno-associated Virus Genome Population Sequencing Achieves Full Vector Genome Resolution and Reveals Human-Vector Chimeras

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Challenges in scaling up AAV-based gene therapy manufacturing

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Undetectable transcription of cap in a clinical AAV vector: implications for preformed capsid in immune responses

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Pulmonary Targeting of Adeno-associated Viral Vectors by Next-generation Sequencing-guided Screening of Random Capsid Displayed Peptide Libraries

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Understanding Capsid Assembly and Genome Packaging for Adeno-Associated Viruses

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Functional Rescue of Dystrophin Deficiency in Mice Caused by Frameshift Mutations Using Campylobacter jejuni Cas9

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A Review of Tangential Flow Filtration: Process Development and Applications in the Pharmaceutical Industry

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