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AAV9 targets cone photoreceptors in the nonhuman primate retina

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Recombinant adeno-associated virus type 2-mediated gene delivery into the Rpe65 -/- knockout mouse eye results in limited rescue

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The role of hypoxia-inducible factors in neovascular age-related macular degeneration: a gene therapy perspective

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Gene therapy prevents photoreceptor death and preserves retinal function in a Bardet-Biedl syndrome mouse model

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Gene supplementation therapy for recessive forms of inherited retinal dystrophies

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Gene Therapy in a Large Animal Model of PDE6A-Retinitis Pigmentosa

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Tetracycline-Inducible Viral Interleukin-10 Intraocular Gene Transfer, Using Adeno-Associated Virus in Experimental Autoimmune Uveoretinitis

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Immune responses to gene editing by viral and non-viral delivery vectors used in retinal gene therapy

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Self-complementary AAV5 vector facilitates quicker transgene expression in photoreceptor and retinal pigment epithelial cells of normal mouse

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Postsurgical Assessment and Long-term Safety of Recombinant Adeno-Associated Virus–Mediated Gene Transfer Into the Retinas of Dogs and Primates

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Adeno-Associated Virus Mediated Gene Therapy for Retinal Degenerative Diseases

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Recombinant adeno-associated virus targets passenger gene expression to cones in primate retina

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Targeting Herpetic Keratitis by Gene Therapy

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Subretinal Delivery and Electroporation in Pigmented and Nonpigmented Adult Mouse Eyes

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Optimized Subretinal Injection Technique for Gene Therapy Approaches

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Differential targeting of feline photoreceptors by recombinant adeno-associated viral vectors: implications for preclinical gene therapy trials

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Longitudinal evaluation of expression of virally delivered transgenes in gerbil cone photoreceptors

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Basic and Clinical Aspects of Gene Therapy for Retinopathy Induced by Diabetes

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Safety of intravitreally delivered AAV2 vector‐mediated multi‐characteristic opsin genetic construct in wild type beagle dogs

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Stable transgene expression in rod photoreceptors after recombinant adeno-associated virus-mediated gene transfer to monkey retina

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Postsurgical Assessment and Long-term Safety of Recombinant Adeno-Associated Virus–Mediated Gene Transfer Into the Retinas of Dogs and Primates

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