Effect of gene therapy on visual function in Leber’s congenital amaurosis

Cited by (1,016)

Items 1,001–1,016 of 1,016

1. An innate immune response to adeno-associated virus genomes decreases cortical dendritic complexity and disrupts synaptic transmission
   Suriano, Christos M., Kumar, Neerav, Verpeut, Jessica L., Ma, Jie, Jung, Caroline, Dunn, Connor E., Carvajal, Brigett V., Nguyen, Ai Vy, Boulanger, Lisa M. · 2024 · Molecular Therapy
2. Perspectives on Gene Therapy: Choroideremia Represents a Challenging Model for the Treatment of Other Inherited Retinal Degenerations
   MacDonald, Ian M., Moen, Christopher, Duncan, Jacque L., Tsang, Stephen H., Cehajic-Kapetanovic, Jasmina, Aleman, Tomas S. · 2020 · Translational Vision Science & Technology
3. Directed Evolution of AAV Targeting Primate Retina by Intravitreal Injection Identifies R100, a Variant Demonstrating Robust Gene Delivery and Therapeutic Efficacy in Non-Human Primates
   Kotterman, Melissa, Beliakoff, Ghezal, Croze, Roxanne, Vazin, Tandis, Schmitt, Christopher, Szymanski, Paul, Leong, Meredith, Quezada, Melissa, Holt, Jenny, Barglow, Katherine et al. · 2021
4. AAV Provides an Alternative for Gene Therapy of the Peripheral Sensory Nervous System
   Beutler, Andreas S · 2010 · Molecular Therapy
5. Regulation of retinal function but nonrescue of vision in RPE65-deficient dogs treated with doxycycline-regulatable AAV vectors
   Lhériteau, Elsa, Libeau, Lyse, Mendes-Madeira, Alexandra, Deschamps, Jack-Yves, Weber, Michel, Le Meur, Guylène, Provost, Nathalie, Guihal, Caroline, Moullier, Philippe, Rolling, Fabienne · 2010 · Molecular Therapy
6. Visual field variability after gene therapy for Leber’s hereditary optic neuropathy
   Yuan, Jia-jia, Zhang, Yong, Wang, Li-ling, Cheng, Ming-shi, Ma, Si-qi, Gao, Qin, Li, Bin · 2018 · Ophthalmic Research
7. Trans-ocular Electric Current In Vivo Enhances AAV-Mediated Retinal Gene Transduction after Intravitreal Vector Administration
   Song, Hongman, Bush, Ronald A., Zeng, Yong, Qian, Haohua, Wu, Zhijian, Sieving, Paul A. · 2019 · Molecular Therapy - Methods & Clinical Development
8. Postnatal eye size in mice is controlled by SREBP2-mediated transcriptional repression of <i>Lrp2</i> and <i>Bmp2</i>
   Mai, Shuyi, Zhu, Xiaoxuan, Wan, Esther Yi Ching, Wu, Shengyu, Yonathan, Jesslyn Nagalin, Wang, Jun, Li, Ying, Ma, Jessica Yuen Wuen, Zuo, Bing, Tse, Dennis Yan-yin et al. · 2022 · Development
9. Correction: AAV9 Targets Cone Photoreceptors in the Nonhuman Primate Retina
   Vandenberghe, Luk H., Bell, Peter, Maguire, Albert M., Xiao, Ru, Hopkins, Tim B., Grant, Rebecca, Bennett, Jean, Wilson, James M. · 2013 · PLoS ONE
10. The road towards gene therapy for X-linked juvenile retinoschisis: a systematic review of preclinical gene therapy in cell-based and rodent models of xlrs
    van der Veen, Isa, Heredero Berzal, Andrea, Koster, Céline, ten Asbroek, Anneloor L. M. A., Bergen, Arthur A., Boon, Camiel J. F. · 2024 · International Journal of Molecular Sciences
11. Subretinal Gene Delivery Using Helper-Dependent Adenoviral Vectors
    Wu, Linda, Lam, Simon, Cao, Huibi, Guan, Rui, Duan, Rongqi, van der Kooy, Derek, Bremner, Rod, Molday, Robert S, Hu, Jim · 2011 · Cell &amp; Bioscience
12. Outer retinal transduction by AAV2-7m8 following intravitreal injection in a sheep model of CNGA3 achromatopsia
    Ross, M., Obolensky, A., Averbukh, E., Desrosiers, M., Ezra-Elia, R., Honig, H., Yamin, E., Rosov, A., Dvir, H., Gootwine, E. et al. · 2022 · Gene Therapy
13. Adeno-Associated Virus D-Sequence-Mediated Suppression of Expression of a Human Major Histocompatibility Class II Gene: Implications in the Development of Adeno-Associated Virus Vectors for Modulating Humoral Immune Response
    Kwon, Hyung-Joo, Qing, Keyun, Ponnazhagan, Selvarangan, Wang, Xu-Shan, Markusic, David M., Gupte, Siddhant, Boye, Shannon E., Srivastava, Arun · 2020 · Human Gene Therapy
14. AAV-mediated gene augmentation therapy restores critical functions in mutant iPSC-derived PRPF31 ^+/- cells
    Brydon, Elizabeth M., Bronstein, Revital, Buskin, Adriana, Lako, Majlinda, Pierce, Eric A., Fernandez-Godino, Rosario · 2019
15. Prevention and inhibition of adverse humoral immune response to gene therapy mediated by adeno-associated virus (AAV) vector
    Meliani, Amine · 2026
16. Untitled work
    1999 · 10.1002/1529-0131(199901)42:1