Effect of gene therapy on visual function in Leber’s congenital amaurosis

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Items 101–200 of 1,016

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15. Vision 1 Year after Gene Therapy for Leber's Congenital Amaurosis
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16. Interim results of a multicenter trial with the new electronic subretinal implant Alpha AMS in 15 Patients blind from inherited retinal degenerations.
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17. NMNAT1 mutations cause Leber congenital amaurosis
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25. Vector platforms for gene therapy of inherited retinopathies
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30. Efficacy and Safety of rAAV2-ND4 Treatment for Leber’s Hereditary Optic Neuropathy
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