Effect of gene therapy on visual function in Leber’s congenital amaurosis

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Items 801–900 of 1,016

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18. Pupillometric analysis for assessment of gene therapy in Leber Congenital Amaurosis patients
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19. Leber congenital amaurosis caused by Lebercilin (LCA5) mutation: retained photoreceptors adjacent to retinal disorganization.
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27. Voretigene Neparvovec and Gene Therapy for Leber’s Congenital Amaurosis: Review of Evidence to Date
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32. Novel RPE65 mutations associated with Leber congenital amaurosis in Chinese patients.
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35. Gene Therapy for the Retinal Degeneration of Usher Syndrome Caused by Mutations in MYO7A
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37. Gene Therapy for Inherited Retinal Degeneration
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38. Helper-dependent adenovirus transduces the human and rat retina but elicits an inflammatory reaction when delivered subretinally in rats
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39. RPE65 Mutations in Two Japanese Families with Leber Congenital Amaurosis
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40. Recombinant adeno-associated Virus: Clinical Application and Development As a gene-therapy Vector
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45. Investigation of PTC124-mediated translational readthrough in a retinal organoid model of AIPL1-associated Leber congenital amaurosis
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