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784. B-Cell Ablation is Protective Against Anti-AAV Capsid Immune Response: A Human Subject Case Study

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Immune Response Mechanisms against AAV Vectors in Animal Models

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Immunomodulation in Administration of RAAV: Preclinical and Clinical Adjuvant Pharmacotherapies

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Single-Dose Intrathecal Dorsal Root Ganglia Toxicity of Onasemnogene Abeparvovec in Cynomolgus Monkeys

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Five Years of Successful Inducible Transgene Expression Following Locoregional Adeno-Associated Virus Delivery in Nonhuman Primates with No Detectable Immunity

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Long-term safety and efficacy of AAV gene therapy in the canine model of glycogen storage disease type Ia

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rAAV8 and rAAV9-Mediated Long-Term Muscle Transduction with Tacrolimus (FK506) in Non-Human Primates

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rAAVrh74.MCK.GALGT2 Demonstrates Safety and Widespread Muscle Glycosylation after Intravenous Delivery in C57BL/6J Mice

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An Isolated Limb Infusion Method Allows for Broad Distribution of rAAVrh74.MCK.GALGT2 to Leg Skeletal Muscles in the Rhesus Macaque

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Short-term treatment of golden retriever muscular dystrophy (GRMD) dogs with rAAVrh74.MHCK7.GALGT2 induces muscle glycosylation and utrophin expression but has no significant effect on muscle strength

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Soluble Heparin Binding Epidermal Growth Factor-Like Growth Factor Is a Regulator of GALGT2 Expression and GALGT2 -Dependent Muscle and Neuromuscular Phenotypes

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Prednisolone and rapamycin reduce the plasma cell gene signature and may improve AAV gene therapy in cynomolgus macaques

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Immunosuppression reduces rAAV2.5T neutralizing antibodies that limit efficacy following repeat dosing to ferret lungs

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Transient rapamycin treatment avoids unwanted host immune responses toward AAV-delivered anti-HIV antibodies

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Biochemical Correction of GM2 Ganglioside Accumulation in AB-Variant GM2 Gangliosidosis

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Prophylactic Prednisolone Promotes AAV5 Hepatocyte Transduction Through the Novel Mechanism of AAV5 Coreceptor Platelet-Derived Growth Factor Receptor Alpha Upregulation and Innate Immune Suppression

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Overcoming Immunological Challenges to Helper-Dependent Adenoviral Vector-Mediated Long-Term CFTR Expression in Mouse Airways

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Immune-driven gene expression loss following intramuscular AAV delivery to non-human primates is only transient

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Optogenetic Control of Muscles: Potential Uses and Limitations

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The Use of AAV Vector-based Gene Therapy in the Treatment of Ophthalmic Diseases. Literature Review

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Balance entre rejet et tolérance : la bipolarité immunitaire du muscle squelettique face à l’AAV recombinant : décryptage de la réponse immune de l’hôte dirigée contre le produit du transgène après injection de vecteurs AAV recombinants par voie intramusculaire

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Evaluation of early prophylactic corticosteroid administration on early safety and efficacy outcomes of adeno-associated virus gene therapy in the hemophilia dog model

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Prednisolone therapy reduces incidence of mononuclear T-cell infiltrates after AAV transduction of GALGT2 in the rhesus macaque

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Human Treg responses allow sustained recombinant adeno-associated virus–mediated transgene expression

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AAV8 Induces Tolerance in Murine Muscle as a Result of Poor APC Transduction, T Cell Exhaustion, and Minimal MHCI Upregulation on Target Cells

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The co-delivery of Programmed Death 1 ligands enhances and prolongs rAAV-mediated gene expression in pre-immunized mice

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