Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy
Cartier, Nathalie, Hacein-Bey-Abina, Salima, Bartholomae, Cynthia C., Veres, Gabor, Schmidt, Manfred, Kutschera, Ina, Vidaud, Michel, Abel, Ulrich, Dal-Cortivo, Liliane, Caccavelli, Laure, Mahlaoui, Nizar, Kiermer, Véronique, Mittelstaedt, Denice, Bellesme, Céline, Lahlou, Najiba, Lefrère, François, Blanche, Stéphane, Audit, Muriel, Payen, Emmanuel, Leboulch, Philippe, l’Homme, Bruno, Bougnères, Pierre, Von Kalle, Christof, Fischer, Alain, Cavazzana-Calvo, Marina, Aubourg, Patrick·2009·Science
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