Genetically corrected iPSCs as cell therapy for recessive dystrophic epidermolysis bullosa

Distinct fibroblast lineages determine dermal architecture in skin development and repair

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Epidermolysis bullosa and the risk of life-threatening cancers: The National EB Registry experience, 1986-2006

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iPS cells: a game changer for future medicine

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High-Efficiency FLP and ΦC31 Site-Specific Recombination in Mammalian Cells

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Generation of keratinocytes from normal and recessive dystrophic epidermolysis bullosa-induced pluripotent stem cells

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Excision of Reprogramming Transgenes Improves the Differentiation Potential of iPS Cells Generated with a Single Excisable Vector

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Potential of Fibroblast Cell Therapy for Recessive Dystrophic Epidermolysis Bullosa

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Collagen VII plays a dual role in wound healing

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A consensus approach to wound care in epidermolysis bullosa

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A hypomorphic mouse model of dystrophic epidermolysis bullosa reveals mechanisms of disease and response to fibroblast therapy

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Human <i>COL7A1</i> -corrected induced pluripotent stem cells for the treatment of recessive dystrophic epidermolysis bullosa

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In vivo generation of transplantable human hematopoietic cells from induced pluripotent stem cells

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Replenishment of type VII collagen and re-epithelialization of chronically ulcerated skin after intradermal administration of allogeneic mesenchymal stromal cells in two patients with recessive dystrophic epidermolysis bullosa

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Amelioration of epidermolysis bullosa by transfer of wild-type bone marrow cells

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Induced Pluripotent Stem Cells from Individuals with Recessive Dystrophic Epidermolysis Bullosa

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Fibroblast cell therapy enhances initial healing in recessive dystrophic epidermolysis bullosa wounds: results of a randomized, vehicle-controlled trial

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Type VII Collagen Is Required for Ras-Driven Human Epidermal Tumorigenesis

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REPROGRAMMED CELLS FOR DISEASE MODELING AND REGENERATIVE MEDICINE

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Differentiation of Mouse Induced Pluripotent Stem Cells into a Multipotent Keratinocyte Lineage

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Induced pluripotent stem cells from human revertant keratinocytes for the treatment of epidermolysis bullosa

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Normal and Gene-Corrected Dystrophic Epidermolysis Bullosa Fibroblasts Alone Can Produce Type VII Collagen at the Basement Membrane Zone

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Revertant mosaicism in skin: natural gene therapy

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Mechanisms of Fibroblast Cell Therapy for Dystrophic Epidermolysis Bullosa: High Stability of Collagen VII Favors Long-term Skin Integrity

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A phase II randomized vehicle-controlled trial of intradermal allogeneic fibroblasts for recessive dystrophic epidermolysis bullosa

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Progress in Epidermolysis Bullosa Research: Toward Treatment and Cure

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Intravenously Injected Recombinant Human Type VII Collagen Homes to Skin Wounds and Restores Skin Integrity of Dystrophic Epidermolysis Bullosa

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Intravenously Injected Human Fibroblasts Home to Skin Wounds, Deliver Type VII Collagen, and Promote Wound Healing

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Bone Marrow Cell Transfer into Fetal Circulation Can Ameliorate Genetic Skin Diseases by Providing Fibroblasts to the Skin and Inducing Immune Tolerance

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Long-Term Type VII Collagen Restoration to Human Epidermolysis Bullosa Skin Tissue

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Successful therapeutic transplantation of revertant skin in epidermolysis bullosa

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ΔNp63 Is Essential for Epidermal Commitment of Embryonic Stem Cells

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Allogeneic blood and bone marrow cells for the treatment of severe epidermolysis bullosa: repair of the extracellular matrix

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Fibroblasts Show More Potential as Target Cells than Keratinocytes in COL7A1 Gene Therapy of Dystrophic Epidermolysis Bullosa

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Matrix metalloproteinase-7 activates heparin-binding epidermal growth factor-like growth factor in cutaneous squamous cell carcinoma

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Transforming growth factor-beta stimulates collagen VII expression by cutaneous cells in vitro.

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Germline Mutation in EXPH5 Implicates the Rab27B Effector Protein Slac2-b in Inherited Skin Fragility

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HB-EGF Induces COL7A1 Expression in Keratinocytes and Fibroblasts: Possible Mechanism Underlying Allogeneic Fibroblast Therapy in Recessive Dystrophic Epidermolysis Bullosa

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Gene Therapy for Skin DiseasesPreprint

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Progress in Epidermolysis Bullosa Research: Summary of DEBRA International Research Conference 2012

Bruckner‐Tuderman, L., McGrath, J. A., Robinson, E. C., & Uitto, J. (2013) · Journal of Investigative Dermatology · doi:10.1038/jid.2013.127 · Cited by 50 · see citing works

The Role of Systematic Reviews and Meta-analysis in Dermatology

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Differentiation of Human Induced Pluripotent Stem Cells into a Keratinocyte Lineage

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Molecular Heterogeneity of Blistering Disorders: The Paradigm of Epidermolysis Bullosa

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Bone Marrow Stem Cell Therapy for Recessive Dystrophic Epidermolysis Bullosa

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Keratin Intracellular Concentration Revisited: Implications for Keratin Function in Surface Epithelia

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Karyotyping Mouse CellsPreprint

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Epidermolysis bullosa – a group of skin diseases with different causes but commonalities in gene expression

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The Quest to Derive Keratinocytes from Pluripotent Stem Cells

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Advanced drug delivery systems and artificial skin grafts for skin wound healing

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Epidermolysis bullosa

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Human <i>COL7A1</i> -corrected induced pluripotent stem cells for the treatment of recessive dystrophic epidermolysis bullosa

Sebastiano, V., Zhen, H. H., Haddad, B., Bashkirova, E., Melo, S. P., Wang, P., Leung, T. L., Siprashvili, Z., Tichy, A., Li, J., et al. (2014) · Science Translational Medicine · doi:10.1126/scitranslmed.3009540 · Cited by 213 · see citing works

Generation and characterization of hair-bearing skin organoids from human pluripotent stem cells

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3D Bioprinting a human iPSC-derived MSC-loaded scaffold for repair of the uterine endometrium

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Induced pluripotent stem cells from human revertant keratinocytes for the treatment of epidermolysis bullosa

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Autologous Induced Pluripotent Stem Cell–Based Cell Therapies: Promise, Progress, and Challenges

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CRISPR/Cas9-based targeted genome editing for correction of recessive dystrophic epidermolysis bullosa using iPS cells

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Efficient in vivo gene editing using ribonucleoproteins in skin stem cells of recessive dystrophic epidermolysis bullosa mouse model

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Next generation human skin constructs as advanced tools for drug development

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Pathomechanisms of Altered Wound Healing in Recessive Dystrophic Epidermolysis Bullosa

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CRISPR/Cas9-based genetic correction for recessive dystrophic epidermolysis bullosa

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TFAP2C- and p63-Dependent Networks Sequentially Rearrange Chromatin Landscapes to Drive Human Epidermal Lineage Commitment

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Gene Therapy for Epidermolysis Bullosa.

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Skin organoids: a new human model for developmental and translational research

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High Local Concentrations of Intradermal MSCs Restore Skin Integrity and Facilitate Wound Healing in Dystrophic Epidermolysis Bullosa

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Antisense Oligonucleotide-mediated Exon Skipping as a Systemic Therapeutic Approach for Recessive Dystrophic Epidermolysis Bullosa

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Progress toward Treatment and Cure of Epidermolysis Bullosa: Summary of the DEBRA International Research Symposium EB2015

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Minimally invasive and targeted therapeutic cell delivery to the skin using microneedle devices

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Ex Vivo COL7A1 Correction for Recessive Dystrophic Epidermolysis Bullosa Using CRISPR/Cas9 and Homology-Directed Repair

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Highly branched poly(β-amino ester)s for gene delivery in hereditary skin diseases

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Fragility of epidermis in newborns, children and adolescents

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Advancement in management of epidermolysis bullosa

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Gene-Corrected Fibroblast Therapy for Recessive Dystrophic Epidermolysis Bullosa using a Self-Inactivating COL7A1 Retroviral Vector

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Cell therapy for basement membrane-linked diseases

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Microneedle-based cell delivery and cell sampling for biomedical applications

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RNA ‐based therapies for genodermatoses

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Toward Combined Cell and Gene Therapy for GenodermatosesPreprint

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Current topics in Epidermolysis bullosa: Pathophysiology and therapeutic challenges

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The potential of gene therapy for recessive dystrophic epidermolysis bullosa*

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Genetic Disorders of the Extracellular Matrix: From Cell and Gene Therapy to Future Applications in Regenerative Medicine

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Unlocking the Potential of Induced Pluripotent Stem Cells for Wound Healing: The Next Frontier of Regenerative Medicine

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Gene Therapy for Inherited Skin Disorders

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Current Applications for Bioengineered Skin

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Cells and Structures Involved in Hair Follicle Regeneration: An Introduction

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