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Genomic Stability of Self-Complementary Adeno-Associated Virus 2 During Early Stages of Transduction in Mouse Muscle In Vivo

Ren, C., Kumar, S., Shaw, D. R., & Ponnazhagan, S. (2005) · Human Gene Therapy · doi:10.1089/hum.2005.16.1047 · Cited by 30

Co‐vaccination with adeno‐associated virus vectors encoding human papillomavirus 16 L1 proteins and adenovirus encoding murine GM‐CSF can elicit strong and prolonged neutralizing antibody

Liu, D., Chang, J., Tsao, Y., Huang, C., Kuo, S.-W., & Chen, S. (2004) · International Journal of Cancer · doi:10.1002/ijc.20530 · Cited by 29

Recombinant adeno-associated virus vector design and gene expression in the mammalian brain

Paterna, J., & Büeler, H. (2002) · Methods · doi:10.1016/s1046-2023(02)00225-6 · Cited by 29

Strategies to improve safety profile of AAV vectors

Suoranta, T., Laham-Karam, N., & Ylä‐Herttuala, S. (2022) · Frontiers in Molecular Medicine · doi:10.3389/fmmed.2022.1054069 · Cited by 32

In vivo engineering of murine T cells using the evolved adeno-associated virus variant Ark313

Nyberg, W. A., Wang, C. H., Ark, J., Liu, C., Clouden, S., Qualls, A., Caryotakis, S. E., Wells, E., Simon, K. E., Garza, C., et al. (2025) · Immunity · doi:10.1016/j.immuni.2025.01.009 · Cited by 32

Adeno-Associated Viral Vector 2 and 9 Transduction Is Enhanced in Streptozotocin-Induced Diabetic Mouse Retina

Lee, S. H., Yang, J. Y., Madrakhimov, S. B., Park, H. Y., Park, K., & Park, T. K. (2018) · Molecular Therapy — Methods & Clinical Development · doi:10.1016/j.omtm.2018.11.008 · Cited by 28

Ring finger protein 121 is a potent regulator of adeno-associated viral genome transcription

Madigan, V. J., Yuziuk, J. A., Chiarella, A. M., Tyson, T. O., Meganck, R. M., Elmore, Z. C., Tse, L. V., Hathaway, N. A., & Asokan, A. (2019) · PLoS Pathogens · doi:10.1371/journal.ppat.1007988 · Cited by 28

Obstacles to human hematopoietic stem cell transduction by recombinant adeno-associated virus 2 vectors

Srivastava, A. (2002) · Journal of Cellular Biochemistry · doi:10.1002/jcb.10053 · Cited by 28

Overexpression of Cyclin A Inhibits Augmentation of Recombinant Adeno-Associated Virus Transduction by the Adenovirus E4orf6 Protein

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Gene Transfer Approaches to the Lysosomal Storage Disorders

Barranger, J. A., Rice, E. O., & Swaney, W. P. (1999) · Neurochemical Research · doi:10.1023/a:1022548232735 · Cited by 28

AAV-mediated gene therapy for liver diseases: the prime candidate for clinical application?

van der Laan, L. J. W., Wang, Y., Tilanus, H. W., Janssen, H. L. A., & Pan, Q. (2011) · Expert Opinion on Biological Therapy · doi:10.1517/14712598.2011.548799 · Cited by 29

Recombinant AAV-directed gene therapy for type I glycogen storage diseases

CHOU, J. Y., & Mansfield, B. C. (2011) · Expert Opinion on Biological Therapy · doi:10.1517/14712598.2011.578067 · Cited by 28

Self-complementary adeno-associated viral vectors for gene therapy of hemophilia B: progress and challenges

Raj, D., Davidoff, A. M., & Nathwani, A. C. (2011) · Expert Review of Hematology · doi:10.1586/ehm.11.48 · Cited by 28

Effects of self-complementarity, codon optimization, transgene, and dose on liver transduction with AAV8

Bell, P., Wang, L., Chen, S.-J., Yu, H., Zhu, Y., Nayal, M., He, Z., White, J., Lebel-Hagan, D., & Wilson, J. M. (2016) · Human Gene Therapy Methods · doi:10.1089/hgtb.2016.039 · Cited by 26

AAV Recombineering with Single Strand Oligonucleotides

Hirsch, M. L., Storici, F., Li, C., Choi, V. W., & Samulski, R. J. (2009) · PLoS ONE · doi:10.1371/journal.pone.0007705 · Cited by 26

Transactivation of human parvovirus B19 gene expression in endothelial cells by adenoviral helper functions

Pozzuto, T., von Kietzell, K., Bock, C. –., Schmidt‐Lucke, C., Poller, W. C., Zobel, T., Laßner, D., Zeichhardt, H., Weger, S., & Fechner, H. (2011) · Virology · doi:10.1016/j.virol.2010.12.019 · Cited by 27

The emerging role of viral vectors as vehicles for DMD gene editing

Maggio, I., Chen, X., & Gonçalves, M. A. F. V. (2016) · Genome Medicine · doi:10.1186/s13073-016-0316-x · Cited by 27

Transduction with recombinant adeno-associated virus for gene therapy is limited by leading-strand synthesis

Fisher, K. J., Gao, G. P., Weitzman, M. D., DeMatteo, R. P., Burda, J. F., & Wilson, J. M. (1996) · Journal of Virology · doi:10.1128/jvi.70.1.520-532.1996 · Cited by 546

Intracellular Viral Processing, Not Single-Stranded DNA Accumulation, Is Crucial for Recombinant Adeno-Associated Virus Transduction

Hauck, B., Zhao, W., High, K. A., & Xiao, W. (2004) · Journal of Virology · doi:10.1128/jvi.78.24.13678-13686.2004 · Cited by 101

Single-polarity Recombinant Adeno-associated Virus 2 Vector-mediated Transgene Expression In Vitro and In Vivo: Mechanism of Transduction

Li, Z., Zhou, X., Li, Y., Qing, K., Xiao, X., Samulski, R. J., & Srivastava, A. (2007) · Molecular Therapy · doi:10.1038/sj.mt.6300376 · Cited by 43

Strategies for improving the transduction efficiency of single-stranded adeno-associated virus vectors in vitro and in vivo

Jayandharan, G. R., Zhong, L., Li, B., Kachniarz, B., & Srivastava, A. (2008) · Gene Therapy · doi:10.1038/gt.2008.89 · Cited by 37

Adeno-Associated Virus Capsid Proteins May Play a Role in Transcription and Second-Strand Synthesis of Recombinant Genomes

Salganik, M., Aydemir, F., Nam, H.-J., McKENNA, R. V., Agbandje‐McKenna, M., & Muzyczka, N. (2013) · Journal of Virology · doi:10.1128/jvi.02093-13 · Cited by 73