Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo
Yin, Hao, Song, Chun-Qing, Dorkin, Joseph R, Zhu, Lihua J, Li, Yingxiang, Wu, Qiongqiong, Park, Angela, Yang, Junghoon +14 more·2016·Nature Biotechnology
DOI 10.1038/nbt.3471
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