Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo

Cited by (874)

Items 601–700 of 874

1. Self-cleaving guide RNAs enable pharmacological selection of precise gene editing events in vivo
   Amita Tiyaboonchai, Anne Vonada, Jeffrey Posey, Carl Pelz, Leslie Wakefield, Markus Grompe · 2022 · Nature Communications
2. Progress in and Prospects of Genome Editing Tools for Human Disease Model Development and Therapeutic Applications
   Hong Thi Lam Phan, Kyoungmi Kim, Ho Lee, Je Kyung Seong · 2023 · Genes
3. Utilization of CRISPR/Cas9 gene editing in cellular therapies for lymphoid malignancies
   Maryam Mehravar, Elham Roshandel, Maryam Salimi, Rouzbeh Chegeni, Majid Gholizadeh, Mohammad Hossein Mohammadi, Abbas Hajifathali · 2020 · Immunology Letters
4. Remaining Challenges in the Treatment of Tyrosinemia from the Clinician’s Viewpoint
   Grant A. Mitchell, Hao Yang · 2017 · Advances in experimental medicine and biology
5. CRISPR/Cas systems usher in a new era of disease treatment and diagnosis
   Ruiting Li, Qin Wang, Kaiqin She, Fang Lu, Yang Yang · 2022 · Molecular Biomedicine
6. The present and future of genome editing in cancer research
   Xiaoyi Li, Riga Wu, Andrea Ventura · 2016 · Human Genetics
7. CRISPR/Cas9: A Potential Life-Saving Tool. What’s next?
   Diana Gulei, Ioana Berindan‐Neagoe · 2017 · Molecular Therapy — Nucleic Acids
8. Non-viral Methodology for Efficient Co-transfection
   Jessica A. Kretzmann, Cameron W. Evans, Marck Nörret, Pilar Blancafort, K. Swaminathan Iyer · 2018 · Methods in molecular biology
9. A Broad Application of CRISPR Cas9 in Infectious Diseases of Central Nervous System
   Anna Bellizzi, Nicholas Ahye, Gauthami S. Jalagadugula, Hassen S. Wollebo · 2019 · Journal of Neuroimmune Pharmacology
10. Epigenetic Editing in Prostate Cancer: Challenges and Opportunities
    Mariana Brütt Pacheco, Vânia Camilo, Rui Henrique, Cármen Jerónimo · 2021 · Epigenetics
11. Think Big, Start Small: How Nanomedicine Could Alleviate the Burden of Rare CNS Diseases
    Abdelfattah Faouzi, Gaëlle Roullin · 2021 · Pharmaceuticals
12. The role of the CRISPR‐Cas system in cancer drug development: Mechanisms of action and therapy
    Arun Pandian Chandrasekaran, Janardhan Keshav Karapurkar, Hee Yong Chung, Suresh Ramakrishna · 2022 · Biotechnology Journal
13. Lipid Nanoparticles for mRNA Delivery in Cancer Immunotherapy
    Yasir Alshehry, Xiang Liu, Wenhua Li, Qiyan Wang, Janét Cole, Guizhi Zhu · 2025 · The AAPS Journal
14. CRISPR/Cas9 Knockout of Bak Mediates Bax Translocation to Mitochondria in response to TNFα/CHX-induced Apoptosis
    Jingtian Zhang, Han Niu, Zhizhuang Joe Zhao, Xueqi Fu, Yuxiang Wang, Xu Zhang, Fuqiang Zhang, Linlin Zeng · 2019 · BioMed Research International
15. Translating genomic insights into cardiovascular medicine: Opportunities and challenges of CRISPR-Cas9
    Yuan Zhang, Ioannis Karakikes · 2020 · Trends in Cardiovascular Medicine
16. CRISPR-Based Tools for Fighting Rare Diseases
    Qingyang Li, Yanmin Gao, Haifeng Wang · 2022 · Life
17. Expression of PTEN ‐long mediated by CRISPR /Cas9 can repress U87 cell proliferation
    Na Fang, Tingxuan Gu, Yahui Wang, Shuzhen Wang, Fengling Wang, Yang An, Wenqiang Wei, Weijuan Zhang, Xiangqian Guo, Adil J. Nazarali et al. · 2017 · Journal of Cellular and Molecular Medicine
18. Emerging treatments and personalised medicine for ciliopathies associated with cystic kidney disease
    Elisa Molinari, John Andrew Sayer · 2017 · Expert Opinion on Orphan Drugs
19. Applications of CRISPR-Cas9 Technology in Translational Research on Solid-Tumor Cancers
    Patricia A. Chen, Liting You, You Lü · 2018 · The CRISPR Journal
20. Unlocking the potential of CRISPR technology for improving livelihoods in Africa
    Reagan Mudziwapasi, Abigarl Ndudzo, Rutendo Patricia Nyamusamba, Fortune Ntengwa Jomane, Tendai Trudor Mutengwa, Mcebisi Maphosa · 2018 · Biotechnology and Genetic Engineering Reviews
21. Biodegradable nano-organosilica gene carrier for high-efficiency gene transfection
    Kun Zeng, Li Ma, Wenxiu Yang, Shan Lei, Mozhen Wang, Ye‐Zi You, Yu Zhao, Xuewu Ge · 2020 · Journal of Materials Chemistry B
22. Genome-wide CRISPR screens for the identification of therapeutic targets for cancer treatment
    Vivian Weiwen Xue, Sze Chuen Cesar Wong, William Chi Shing Cho · 2020 · Expert Opinion on Therapeutic Targets
23. Postnatal therapeutic approaches in genetic neurodevelopmental disorders
    Gilad Levy, Boaz Barak · 2020 · Neural Regeneration Research
24. Applications and challenges of biomaterial mediated mRNA delivery
    Huapan Fang, Qian Chen · 2022 · Exploration of Targeted Anti-tumor Therapy
25. Saponin and fluorine-modified polycation as a versatile gene delivery system
    Akbar Hasanzadeh, Amir Hossein Vahabi, Seyyed Emad Hooshmand, Elaheh Sadat Hosseini, Behjat Kheiri Yeghaneh Azar, Jafar Kiani, Sara Saeedi, Ali Shahbazi, Arnab Rudra, Michael Richard Hamblin et al. · 2022 · Nanotechnology
26. DNA base editing corrects common hemophilia A mutations and restores factor VIII expression in in vitro and ex vivo models
    Elena Tonetto, Alessia Cucci, Antonia Follenzi, Francesco Bernardi, Mirko Pinotti, Dario Balestra · 2024 · Journal of Thrombosis and Haemostasis
27. Brain‐Targeted Cas12a Ribonucleoprotein Nanocapsules Enable Synergetic Gene Co‐Editing Leading to Potent Inhibition of Orthotopic Glioblastoma
    Weimin Ruan, Sen Xu, Yang An, Yingxue Cui, Yang Liu, Yibin Wang, Muhammad Ismail, Yong Liu, Meng Zheng · 2024 · Advanced Science
28. Engineering branched ionizable lipid for hepatic delivery of clustered regularly interspaced short palindromic repeat-Cas9 ribonucleoproteins
    Haruno Onuma, Rina Shimizu, Yuichi Suzuki, Mina Sato, Hideyoshi Harashima, Yusuke Sato · 2024 · iScience
29. Spatiotemporal liver dynamics shape hepatocellular heterogeneity and impact in vivo gene engineering
    Michela Milani, Francesco Starinieri, Stefano Beretta, Marco Monti, Cesare Canepari, Francesca Marabotti, Samuel Zambrano, Davide Mazza, Anna Fabiano, Chiara Simoni et al. · 2025 · Journal of Hepatology
30. Delivery Methods, Resources and Design Tools in CRISPR/Cas
    Muhammad Aamir Aslam, Masooma Hammad, Aftab Ahmad, Josef Altenbuchner, Hazrat Ali · 2021 · Springer eBooks
31. Reversible switching of primary cells between normal and malignant state by oncogenic virus KSHV and CRISPR/Cas9‐mediated targeting of a major viral latent protein
    Enguo Ju, Tingting Li, Suzane Ramos da Silva, Ashley D. Markazi, Shou‐Jiang Gao · 2021 · Journal of Medical Virology
32. Nanoparticle-mediated delivery of non-viral gene editing technology to the brain
    Lucian Williams, Jessica Larsen · 2023 · Progress in Neurobiology
33. Therapeutic nucleic acids in regenerative medicine and tissue repair
    Qimanguli Saiding, Duotian Qin, Soohwan An, Dylan Neal Patel, Muhammad Muzamil Khan, Na Kong, Wei Tao · 2024 · Nano Research
34. Stem Cell Therapy for Fanconi Anemia
    Qing‐Shuo Zhang · 2017 · Advances in experimental medicine and biology
35. CRISPR-Cas9 Therapies in Experimental Mouse Models of Cancer
    Diogo Estêvão, Natália Rios Costa, Rui M. Gil da Costa, Rui Medeiros · 2018 · Future Oncology
36. Applying switchable Cas9 variants to in vivo gene editing for therapeutic applications
    Emily M. Mills, Victoria L. Barlow, Louis Y. P. Luk, Yu‐Hsuan Tsai · 2019 · Cell Biology and Toxicology
37. Viral and Nonviral Transfer of Genetic Materials to Adipose Tissues: Toward a Gold Standard Approach
    Steven M. Romanelli, Ormond A. MacDougald · 2020 · Diabetes
38. CRISPR/Cas9 gene editing: A new hope for transthyretin amyloidosis treatment
    Faizan Shahzad, Mohammad Ebad Ur Rehman, Jawad Basit, Sajeel Saeed, Khawar Abbas, Muhammad Farhan · 2022 · Annals of Medicine and Surgery
39. Nuclear‐Targeting Peptides for Cancer Therapy
    Xuan Yi, Irshad Hussaın, Peng Zhang, Chunsheng Xiao · 2024 · ChemBioChem
40. Nano-enabled pharmacogenomics: revolutionizing personalized drug therapy
    Ruchı Tıwarı, Dhruv Dev, Maharshi Thalla, Vaibhav Dagaji Aher, Anand B. Mundada, Pooja Anand Mundada, Krishna Vaghela · 2024 · Journal of Biomaterials Science Polymer Edition
41. Cancer gene therapy: innovations in therapeutic delivery of CRISPR-Cas9
    Nicole Lindsay‐Mosher, Cathy Su · 2016 · Drug Discovery Today Disease Models
42. An episomal CRISPR/Cas9 system to derive vector-free gene modified mammalian cells
    Linlin Li, Fei Gao, Sen Wu · 2016 · Protein & Cell
43. A zwitterionic polymer-inspired material mediated efficient CRISPR-Cas9 gene editing
    Lingmin Zhang, Langyu Yang, Jionghua Huang, Sheng Chen, Chuangjia Huang, Yinshan Lin, Ao Shen, ZhouYikang Zheng, Wenfu Zheng, Shunqing Tang · 2022 · Asian Journal of Pharmaceutical Sciences
44. Gene editing strategies to treat lysosomal disorders: The example of mucopolysaccharidoses
    Flávia Nathiely Silveira Fachel, Lariane Frâncio, Édina Poletto, Roselena Silvestri Schuh, Hélder Ferreira Teixeira, Roberto Giugliani, Guilherme Baldo, Úrsula da Silveira Matte · 2022 · Advanced Drug Delivery Reviews
45. Synthetic nanoparticles for the delivery of CRISPR/Cas9 gene editing system: classification and biomedical applications
    Qi Zheng, Weitao Wang, Yuhang Zhou, Jiayin Mo, Xinyue Chang, Zhengbao Zha, Lisha Zha · 2023 · Biomaterials Science
46. Synthesis and Characterization of Vitamin D 3 -Functionalized Carbon Dots for Crispr/Cas9 Delivery
    Akbar Hasanzadeh, Fatemeh Radmanesh, Elaheh Sadat Hosseini, Iman Hashemzadeh, Jafar Kiani, Marzieh Naseri, Helena Nourizadeh, Yousef Fatahi, Behjat Kheiri Yeghaneh Azar, Behnaz Golnari Marani et al. · 2021 · Nanomedicine
47. CRISPR/dCas9-mediated cell differentiation
    Jing Gong, Ding Tang, Kam W. Leong · 2018 · Current Opinion in Biomedical Engineering
48. Targeted Gene Insertion: The Cutting Edge of CRISPR Drug Development with Hemophilia as a Highlight
    Zhenjie Zhang, Siqi Zhang, Hoi Ting Wong, Dali Li, Bo Feng · 2024 · BioDrugs
49. Therapeutic Gene Editing in Dyslipidemias
    Seyed Saeed Tamehri Zadeh, Michael David Shapiro · 2024 · Reviews in Cardiovascular Medicine
50. Tuning the tropism and infectivity of SARS-CoV-2 virus-like particles for mRNA delivery
    Qi Yang, Bruce A. Davidson, Petar Pajic, Xuyang Chen, Ömer Gökçümen, Min Gao, Sriram Neelamegham · 2025 · Nucleic Acids Research
51. Strategies and mechanisms of precision genome engineering: From gene editing to genome writing
    Kerui Huang, Jianhong Tian, Wenyan Zhao, Siqin Zhang, Lixuan Xiang, Meiqing Yang, Liu Ls, Y Huang, Ningyun Zhang, Lei Sun et al. · 2026 · iMetaOmics.
52. Genome editing for the reproduction and remedy of human diseases in mice
    Satoshi Hara, Shuji Takada · 2017 · Journal of Human Genetics
53. CRISPR/Cas-based Diagnostics and Gene Therapy
    Meiyu Qiu, Pei Li · 2021 · BIO Integration
54. Challenges and Future Prospects of CRISPR Technology
    Zulqurnain Khan, Sultan Habibullah Khan, Aftab Ahmad · 2021 · Springer eBooks
55. Influence of Hydrophobicity in the Hydrophilic Region of Cationic Lipids on Enhancing Nucleic Acid Delivery and Gene Editing
    Hithavani Rapaka, Shireesha Manturthi, Porkizhi Arjunan, Vigneshwaran Venkatesan, Saravanabhavan Thangavel, Srujan Kumar Marepally, Srilakshmi V. Patri · 2022 · ACS Applied Bio Materials
56. Genome Editing in Ferret Airway Epithelia Mediated by CRISPR/Nucleases Delivered with Amphiphilic Shuttle Peptides
    Meihui Luo, Jia Ma, Xue Cheng, Shuang Wu, D. Bartels, David R.P. Guay, John F. Engelhardt, Xiaoming Liu · 2023 · Human Gene Therapy
57. Recent advances in CRISPR-Cas systems for colorectal cancer research and therapeutics
    Saeideh Khorshid Sokhangouy, Farzaneh Lal Alizadeh, Malihe Lotfi, Samaneh Sharif, Atefeh Ashouri, Yasamin Yoosefi, Saeed Bozorg Qomi, Mohammad Reza Abbaszadegan · 2024 · Expert Review of Molecular Diagnostics
58. Retinoid dynamics in vision: from visual cycle biology to retina disease treatments
    Jaclyn Swigris, Made Airanthi K. Widjaja‐Adhi, Marcin Golczak · 2025 · Pharmacology & Therapeutics
59. CRISPR Editing in Biological and Biomedical Investigation
    Han Zhang, Nami McCarty · 2017 · Journal of Cellular Biochemistry
60. Using Genome Engineering to Understand Huntington’s Disease
    Barbara J. Bailus, Ningzhe Zhang, Lisa Ellerby · 2017 · Research and perspectives in neurosciences
61. Targeted Gene Editing in Human Pluripotent Stem Cells Using Site-Specific Nucleases
    Sylvia Merkert, Ulrich Martin · 2017 · Advances in biochemical engineering, biotechnology
62. Advances in CRISPR/Cas9 Technology for in Vivo Translation
    Yağız Anıl Çiçek, David C. Luther, Jessica A. Kretzmann, Vincent M. Rotello · 2019 · Biological and Pharmaceutical Bulletin
63. Will CRISPR-Cas9 Have Cards to Play Against Cancer? An Update on its Applications
    Daisy Precilla Senthilathiban, Shreyas S. Kuduvalli, T. S. Anitha · 2021 · Molecular Biotechnology
64. Therapeutic perspectives for structural and functional abnormalities of cilia
    Yong Joon Kim, Joon Kim · 2019 · Cellular and Molecular Life Sciences
65. Genome Editing: Insights from Chemical Biology to Support Safe and Transformative Therapeutic Applications
    Renee D. Wegrzyn, Andrew H. Lee, Amy L. Jenkins, Colby D. Stoddard, Anne E. Cheever · 2017 · ACS Chemical Biology
66. Prime editing enables precise genome editing in mouse liver and retina
    Hyewon Jang, Jeong Hong Shin, Dong Hyun Jo, Jung Hwa Seo, Goosang Yu, Ramu Gopalappa, Sung‐Rae Cho, Jeong Hun Kim, Seokjoong Kim · 2021 · bioRxiv (Cold Spring Harbor Laboratory)
67. SETDB1 promotes mammalian liver regeneration by stimulating cytokine CSF3 in hepatocytes
    Xiaoyan Huang, Dong Yang, Yinzhe Liu, Enxiang Zhang, Qiao Yang, Wang Kang, Xiao-Ou Zhang, Junwei Shi, Chun‐Qing Song · 2025 · Cell Reports
68. CRISPR-Cas technologies: Emerging tools from research to clinical application
    Hana Hyeon, Soonhye Hwang, Yongyang Luo, Eunkyoung Shin, Ji‐Hyun Yeom, Hong‐Man Kim, Minkyung Ryu, Kangseok Lee · 2025 · The Journal of Microbiology
69. Treating Cardiovascular Disease with Liver Genome Engineering
    Ayrea E. Hurley, William R. Lagor · 2022 · Current Atherosclerosis Reports
70. Application of CRISPR-Cas9 Technology in Fish
    Nilav Aich, Janmejay Parhi, Sagar Chandra Mandal, Lopamudra Sahoo · 2023 · Springer eBooks
71. Rescue of the endogenous FVIII expression in hemophilia A mice using CRISPR-Cas9 mRNA LNPs
    Chun‐Yu Chen, Xiaohe Cai, Barbara A. Konkle, Carol H. Miao · 2024 · Molecular Therapy — Nucleic Acids
72. Gene therapy: Myth or reality?
    Alain Fischer · 2016 · Comptes Rendus Biologies
73. Supramolecular Gene Transfection Agents
    Bruno Pitard, Damien Habrant · 2016 · Elsevier eBooks
74. Modular Synthesis of Bioreducible Gene Vectors through Polyaddition of N,N′-Dimethylcystamine and Diglycidyl Ethers
    Guoying Si, M. Rachèl Elzes, Johan F. J. Engbersen, Jos M. J. Paulusse · 2018 · Polymers
75. Genome editing in the human liver: Progress and translational considerations
    Samantha L. Ginn, Sharntie Christina, Ian E. Alexander · 2021 · Progress in molecular biology and translational science
76. Comparison of chemically mediated CRISPR/Cas9 gene editing systems using different nonviral vectors in porcine embryos
    Qingyi Lin, Koki Takebayashi, Nanaka Torigoe, Bin Liu, Zhao Namula, Maki Hirata, Fuminori Tanihara, Megumi Nagahara, Takeshige Otoi · 2023 · Animal Science Journal
77. Gene based therapies for kidney regeneration
    Manoe Jacoba Janssen, Fanny Oliveira Arcolino, Perry Schoor, Robbert J. Kok, Enrico Mastrobattista · 2016 · European Journal of Pharmacology
78. Expression of PTEN‑long nephritis and its effect on renal inflammation
    Hui Wang, Qingxia Yu, Lin Wang, Yongwei Li, Mao Xie, Youyi Lu, Yupeng Cui · 2018 · Experimental and Therapeutic Medicine
79. Crispr2vec: Machine Learning Model Predicts Off-Target Cuts of CRISPR systems
    Tara Basu Trivedi, Ron S. Boger, Govinda M. Kamath, Georgios Evangelopoulos, Jamie H. D. Cate, Jennifer A. Doudna, Jack D. Hidary · 2020 · bioRxiv (Cold Spring Harbor Laboratory)
80. CRISPR Technology: Transforming the Future of Medicine and Diagnostics
    Kavita A. Iyer, Rumiana Tenchov, Leilani M. Lotti Diaz, Preeti Jain, Trupti Thite, Yi Deng, Qiongqiong Angela Zhou · 2025 · Biochemistry
81. CD44-targeted lipid nanoparticles for enhanced CRISPR/Cas9 delivery in cancer gene editing
    Ye Zeng, Gangyin Zhao, Shidi Wu, Hu Bochuan, Gabriel Forn‐Cuní, Renzo A. Knol, Abdoelwaheb El Ghalbzouri, Ewa B. Snaar-Jagalska, Alexander Kros · 2026 · Journal of Controlled Release
82. Application and Development of CRISPR/Cas9 Technology in Pig Research
    Huafeng Lin, Qiudi Deng, Lili Li, Lei Shi · 2019 · IntechOpen eBooks
83. A Proton‐Activatable DNA‐Based Nanosystem Enables Co‐Delivery of CRISPR/Cas9 and DNAzyme for Combined Gene Therapy
    Feng Li, Nachuan Song, Yuhang Dong, Shuai Li, Linghui Li, Yujie Liu, Zhemian Li, Dayong Yang · 2022 · Angewandte Chemie
84. Enabling Precision Medicine with CRISPR-Cas Genome Editing Technology: A Translational Perspective
    Nazma F. Ilahibaks, Maike J. Hulsbos, Zhiyong Lei, Pieter Vader, Joost P. G. Sluijter · 2022 · Advances in experimental medicine and biology
85. A novel mucopolysaccharidosis type II mouse model with an iduronate-2-sulfatase-P88L mutation
    Ryuichi Mashima, Mari Ohira, Torayuki Okuyama, Masafumi Onodera, Shuji Takada · 2023 · Scientific Reports
86. Modern Approaches to Mouse Genome Editing Using the CRISPR-Cas Toolbox and Their Applications in Functional Genomics and Translational Research
    Cíntia Júnia Monteiro, David M. Heery, Jonathan B. Whitchurch · 2023 · Advances in experimental medicine and biology
87. One-step in vivo gene knock-out in porcine embryos using recombinant adeno-associated viruses
    Mengyu Gao, Yuting He, Xinglong Zhu, Wanliu Peng, Yanyan Zhou, Yang Deng, Guangneng Liao, Wei Min NI, Yi Li, Gao Jun et al. · 2024 · Frontiers in Cell and Developmental Biology
88. Current Progress and Future Prospects in Nucleic Acid Based Therapeutics
    Mayumi M. Takahashi, Si‐ping Han, Lisa J. Scherer, Sorah Yoon, John J. Rossi · 2017 · Elsevier eBooks
89. Potentials of CRISPR in liver research and therapy
    Robin Loesch, Christèle Desbois‐Mouthon, Sabine Colnot · 2018 · Clinics and Research in Hepatology and Gastroenterology
90. Self-Assembled Plasmid Delivery System for PPM1D Knockout to Reverse Tumor Malignancy
    Xiaohe Ren, Xiaoyan He, Boya Liu, Chang Xu, Si‐Xue Cheng · 2020 · ACS Applied Bio Materials
91. Engineering precision therapies: lessons and motivations from the clinic
    Mingqi Xie, Mirta Viviani, Martin Fussenegger · 2020 · Synthetic Biology
92. Gene Therapy in Pediatric Liver Disease
    Andrés Fernando Muro, Lorenzo D’Antiga, Federico Mingozzi · 2019 · Springer eBooks
93. Movement Disorders and Inherited Metabolic Disorders
    2020 · Cambridge University Press eBooks
94. Efficacious genome editing in infant mice with glycogen storage disease type Ia
    Benjamin Arnson, Ekaterina Ilich, Troy von Beck, Songtao Li, Elizabeth Drake Brooks, Dorothy Gheorghiu, Gordon He, Matthew Weinrub, Sze Ying Chan, Hye‐Ri Kang et al. · 2025 · JCI Insight
95. Recent advances in CRISPR/Cas9-assisted gene therapy
    Apeksha Srivastava, Shikha Chauhan, Vishal Ahuja · 2023 · Karbala International Journal of Modern Science
96. CircRNA-based therapeutics: Current opinions and clinical potential
    Hanyuan Liu, Xuelin Yao, Ying Long Zhou, Liang Chen · 2024 · The Innovation Medicine
97. Prenatal Gene Therapy for Metabolic Disorders
    Barbara E. Coons, William H. Peranteau · 2021 · Clinical Obstetrics & Gynecology
98. The Synergy between CRISPR and Chemical Engineering
    Cia‐Hin Lau, Chung Tin · 2019 · Current Gene Therapy
99. Balance between DNA‐binding affinity and specificity enables selective recognition of longer target sequences in vivo
    T. Sunami, Hidetoshi Kono · 2019 · Protein Science
100. Pressing diseases that represent promising targets for gene therapy.
     Marie Beitelshees, Andrew B. Hill, Pooya Rostami, Charles H Jones, Blaine A. Pfeifer · 2017 · PubMed