C9orf72 BAC Transgenic Mice Display Typical Pathologic Features of ALS/FTD

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Aggregation-prone c9FTD/ALS poly(GA) RAN-translated proteins cause neurotoxicity by inducing ER stress

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Hypermethylation of the CpG Island Near the G4C2 Repeat in ALS with a C9orf72 Expansion

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Nucleolar stress and impaired stress granule formation contribute to C9orf72 RAN translation-induced cytotoxicity

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