The DOI matches its Crossref record; 15 of the 15 references it cites were found in a registry or an index.
A pilot study of ex vivo gene therapy for homozygous familial hypercholesterolaemia
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Citations
Cites
A Receptor-Mediated Pathway for Cholesterol Homeostasis
Brown, M. S., & Goldstein, J. L. (1986) · Science · doi:10.1126/science.3513311 · Cited by 5,703
The Metabolic Basis of Inherited Disease
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Molecular genetics of the LDL receptor gene in familial hypercholesterolemia
Hobbs, H. H., Brown, M. S., & Goldstein, J. L. (1992) · Human Mutation · doi:10.1002/humu.1380010602 · Cited by 921
Successful ex vivo gene therapy directed to liver in a patient with familial hypercholesterolaemia
Grossman, M., Raper, S. E., Kozarsky, K., Stein, E. A., Engelhardt, J. F., Muller, D., Lupien, P. J., & Wilson, J. M. (1994) · Nature Genetics · doi:10.1038/ng0494-335 · Cited by 559
Self-citationEpstein, F. H., Goldstein, J. L., Kita, T., & Brown, M. S. (1983) · New England Journal of Medicine · doi:10.1056/nejm198308043090507 · Cited by 469
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Long-Term Improvement of Hypercholesterolemia After Ex Vivo Gene Therapy in LDLR-Deficient Rabbits
Chowdhury, J. R., Grossman, M., Gupta, S., Chowdhury, N. R., Baker, J. R., & Wilson, J. M. (1991) · Science · doi:10.1126/science.1722351 · Cited by 366
Self-citationCommon low-density lipoprotein receptor mutations in the French Canadian population.
Leitersdorf, E., Tobin, E. J., Davignon, J., & Hobbs, H. H. (1990) · Journal of Clinical Investigation · doi:10.1172/jci114531 · Cited by 302
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Self-citationThe low density lipoprotein receptor is not required for normal catabolism of Lp(a) in humans.
Rader, D. J., Mann, W. A., Cain, W., Kraft, H. G., Usher, D., Zech, L. A., Hoeg, J. M., Davignon, J., Lupien, P., & Grossman, M. (1995) · Journal of Clinical Investigation · doi:10.1172/jci117794 · Cited by 176
Self-citationRaper, S. E., S, M. G. B., Rader, D. J., Thoene, J. G., Clark, B. J., Kolansky, D. M., Muller, D. W., & Wilson, J. M. (1996) · Annals of Surgery · doi:10.1097/00000658-199602000-00002 · Cited by 113
Self-citationGordon, B. R., Kelsey, S. F., Bilheimer, D. W., Brown, D. C., Dau, P. C., Gotto, A. M., Illingworth, D. R., Jones, P. H., Leitman, S. F., Prihoda, J. S., et al. (1992) · The American Journal of Cardiology · doi:10.1016/0002-9149(92)90352-y · Cited by 95
Self-citationMalloy, M. J., KANE, J. P., KUNITAKE, S. T., & TUN, P. (1987) · Annals of Internal Medicine · doi:10.7326/0003-4819-107-5-616 · Cited by 88
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Cited by
Naldini, L., Blömer, U., Gage, F. H., Trono, D., & Verma, I. M. (1996) · Proceedings of the National Academy of Sciences · doi:10.1073/pnas.93.21.11382 · Cited by 1,499
Cuchel, M., Bruckert, E., Ginsberg, H. N., Raal, F. J., Santos, R. D., Hegele, R. A., Kuivenhoven, J. A., Nordestgaard, B. G., Descamps, O. S., Steinhagen-Thiessen, E., et al. (2014) · European Heart Journal · doi:10.1093/eurheartj/ehu274 · Cited by 1,057
In vitro models for liver toxicity testing
Soldatow, V. Y., LeCluyse, E. L., Griffith, L. G., & Rusyn, I. (2013) · Toxicol. Res. · doi:10.1039/c2tx20051a · Cited by 472
Hepatocyte Transplantation for the Treatment of Human Disease
Strom, S., Chowdhury, J., & Fox, I. (1999) · Seminars in Liver Disease · doi:10.1055/s-2007-1007096 · Cited by 366
Human hepatocyte transplantation: current experience and future challenges
Dhawan, A., Puppi, J., Hughes, R. D., & Mitry, R. R. (2010) · Nature Reviews Gastroenterology & Hepatology · doi:10.1038/nrgastro.2010.44 · Cited by 362
Metadata
- Authors
- Grossman, M., Rader, D. J., Muller, D. W. M., Kolansky, D. M., Kozarsky, K., Clark, B. J., Stein, E. A., Lupien, P. J., Brewer, H. B., Raper, S. E., & Wilson, J. M.
- Venue
- Nature Medicine
- Published
- 1995-11
- Volume
- 1
- Issue
- 11
- Pages
- 1148-1154
- ISSN
- 1078-8956 (ISSN-L)
- 1546-170X
- OpenAlex
- W2062723580
- Cited by
- 530
- References
- 15
- FWCI
- 12.98
- Type
- journal article
- Language
- en
- Open access
- closed
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Registry, retraction, Cites and statistics results are computed, not judged, with one exception: a printed reference that no index lists is read once by a model before it counts as a citation error. Claims are extracted by a model and kept only when their quote appears verbatim in the text; each cited source is then checked, with a model’s help, for whether it says what the claim relies on. Those verdicts can be wrong — read the claim’s quote and the cited source before relying on one.
Statistics and arithmetic are recomputed, not judged.
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Data sources
Bibliographic data: Semantic Scholar, OpenAlex, Crossref.
Contains information from the Semantic Scholar Academic Graph Datasets, made available under the ODC Attribution License (ODC-BY 1.0).
Semantic Scholar’s data is described in: Kinney, R., et al. (2023). The Semantic Scholar Open Data Platform. arXiv:2301.10140.
