Genome Editing in Primary Cells and in Vivo Using Viral-Derived Nanoblades Loaded with Cas9-SgRNA Ribonucleoproteins

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Organoid Models and Applications in Biomedical Research

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High-Frequency off-Target Mutagenesis Induced by CRISPR-Cas Nucleases in Human Cells

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Easy quantitative assessment of genome editing by sequence trace decomposition

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GUIDE-seq enables genome-wide profiling of off-target cleavage by CRISPR-Cas nucleases

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Dynamic Imaging of Genomic Loci in Living Human Cells by an Optimized CRISPR/Cas System

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Highly efficient Cas9-mediated transcriptional programming

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Cationic lipid-mediated delivery of proteins enables efficient protein-based genome editing in vitro and in vivo

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A Long Noncoding RNA Mediates Both Activation and Repression of Immune Response Genes

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Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo

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Assembly and release of HIV-1 precursor Pr55gag virus-like particles from recombinant baculovirus-infected insect cells

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Structure-guided chemical modification of guide RNA enables potent non-viral in vivo genome editing

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CD81 Is Required for Hepatitis C Virus Glycoprotein-Mediated Viral Infection

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Highly Efficient Mouse Genome Editing by CRISPR Ribonucleoprotein Electroporation of Zygotes

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A localized nucleolar DNA damage response facilitates recruitment of the homology-directed repair machinery independent of cell cycle stagePreprint

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Therapeutic opportunities for manipulating TReg cells in autoimmunity and cancer

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Lentiviral vector retargeting to P-glycoprotein on metastatic melanoma through intravenous injection

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Mystery solved: VSV-G-LVs do not allow efficient gene transfer into unstimulated T cells, B cells, and HSCs because they lack the LDL receptor

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Lentivirus pre-packed with Cas9 protein for safer gene editing

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CRISPRseek: A Bioconductor Package to Identify Target-Specific Guide RNAs for CRISPR-Cas9 Genome-Editing Systems

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Validation of microinjection methods for generating knockout mice by CRISPR/Cas-mediated genome engineering

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Marker-free coselection for CRISPR-driven genome editing in human cells

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Stable transduction of quiescent T cells without induction of cycle progression by a novel lentiviral vector pseudotyped with measles virus glycoproteins

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Baboon envelope pseudotyped LVs outperform VSV-G-LVs for gene transfer into early-cytokine-stimulated and resting HSCs.

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Protein transduction from retroviral Gag precursors

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Reprogramming metabolic pathways in vivo with CRISPR/Cas9 genome editing to treat hereditary tyrosinaemia

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Selective Expression of the Cre Recombinase in Late-Stage Thymocytes Using the Distal Promoter of the Lck Gene

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Protein Transfer Into Human Cells by VSV-G-induced Nanovesicles

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Efficient, footprint-free human iPSC genome editing by consolidation of Cas9/CRISPR and piggyBac technologies

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Streamlined ex vivo and in vivo genome editing in mouse embryos using recombinant adeno-associated viruses

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Density Gradient Centrifugation of a Murine Leukemia Virus

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Exploring treatment options in cancer: tumor treatment strategies

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Engineered Virus-like Particles for Efficient in Vivo Delivery of Therapeutic Proteins

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Therapeutic in vivo delivery of gene editing agents

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Autism genes converge on asynchronous development of shared neuron classes

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Mammalian Retrovirus-like Protein PEG10 Packages Its Own MRNA and Can Be Pseudotyped for MRNA Delivery

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Loop extrusion as a mechanism for formation of DNA damage repair foci

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Recent Advances in CRISPR/Cas9 Delivery Strategies

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In vivo human T cell engineering with enveloped delivery vehicles

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Targeted delivery of CRISPR-Cas9 and transgenes enables complex immune cell engineering

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In vivo somatic cell base editing and prime editing

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Application of CRISPR/Cas9-Based Gene Editing in HIV-1/AIDS Therapy

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Lentiviral delivery of co-packaged Cas9 mRNA and a Vegfa-targeting guide RNA prevents wet age-related macular degeneration in mice

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A Proton‐Activatable DNA‐Based Nanosystem Enables Co‐Delivery of CRISPR/Cas9 and DNAzyme for Combined Gene Therapy

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CRISPR Modeling and Correction of Cardiovascular Disease

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Lentiviral Vector Pseudotypes: Precious Tools to Improve Gene Modification of Hematopoietic Cells for Research and Gene Therapy

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CRISPR technologies for stem cell engineering and regenerative medicine

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