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CRISPR/Cas9 genome surgery for retinal diseases
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“To date, CRISPR/Cas9 has been used to develop animal models, understand disease mechanisms, and validate treatment targets [2,3,4,5].”
From Viral Delivery Systems for CRISPR (2019) · cites this paper as [2]
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Citations
Cites
Effect of genome size on AAV vector packaging
Wu, Z., Yang, H., & Colosi, P. (2010) · Molecular Therapy · doi:10.1038/mt.2009.255 · Cited by 1,029
Beyond editing: repurposing CRISPR-Cas9 for precision genome regulation and interrogation
Dominguez, A. A., Lim, W. A., & Qi, L. S. (2016) · Nature Reviews Molecular Cell Biology · doi:10.1038/nrm.2015.2 · Cited by 832
In vivo genome editing with a small Cas9 orthologue derived from Campylobacter jejuni
Kim, E., Koo, T., Park, S. W., Kim, D., Kim, K., Cho, H.-Y., Song, D. W., Lee, K. J., Jung, M. H., Kim, S., et al. (2017) · Nature Communications · doi:10.1038/ncomms14500 · Cited by 715
DNA repair mechanisms in dividing and non-dividing cells
Iyama, T., & Wilson, D. M. (2013) · DNA Repair · doi:10.1016/j.dnarep.2013.04.015 · Cited by 697
Nrl knockdown by AAV-delivered CRISPR/Cas9 prevents retinal degeneration in mice
Yu, W., Mookherjee, S., Chaitankar, V., Hiriyanna, S., Kim, J.-W., Brooks, M., Ataeijannati, Y., Sun, X., Dong, L., Li, T., et al. (2017) · Nature Communications · doi:10.1038/ncomms14716 · Cited by 271
Genome Editing Abrogates Angiogenesis in Vivo
Huang, X., Zhou, G., Wu, W., Duan, Y., Ma, G., Song, J., Xiao, R., Vandenberghe, L., Zhang, F., D’Amore, P. A., et al. (2017) · Nature Communications · doi:10.1038/s41467-017-00140-3 · Cited by 142
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Cited by
Sorted by citations
Viral Delivery Systems for CRISPR
Xu, C. L., Ruan, M. Z. C., Mahajan, V. B., & Tsang, S. H. (2019) · Viruses · doi:10.3390/v11010028 · Cited by 277
Self-citation
Metadata
- Authors
- Xu, C. L., Park, K. S., & Tsang, S. H.
- Venue
- Drug Discovery Today: Technologies
- Publisher
- Elsevier BV
- Published
- 2018-08
- Volume
- 28
- Pages
- 23-32
- ISSN
- 1740-6749
- PMC
- PMC6136254
- Cited by
- 14
- References
- 6
- Language
- en
- Licence
- Funders
- National Eye Institute, NIH (P30EY019007, R01EY018213, R01EY024698, R01EY026682, R21AG050437)
- National Cancer Institute Core (5P30CA013696)
- Tistou and Charlotte Kerstan Foundation
- Schneeweiss Stem Cell Fund, New York State (C029572)
- Foundation Fighting Blindness New York Regional Research Center Grant (C-NY05-0705-0312)
- Crowley Family Fund
- Gebroe Family Foundation
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