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Adaptive Immune Responses Elicited by Baculovirus and Impacts on Subsequent Transgene Expression In Vivo

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Therapy of Genetic Disorders: Novel Therapies for Duchenne Muscular Dystrophy

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Nanotherapy for Duchenne muscular dystrophy

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The VP1u of Human Parvovirus B19: A Multifunctional Capsid Protein with Biotechnological Applications

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Primary Effect of SERCA2a Gene Transfer on Conduction Reserve in Chronic Myocardial Infarction

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Regenerative medicine improve neurodegenerative diseases

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In Vivo Hematopoietic Stem Cell Genome Editing: Perspectives and Limitations

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Characterization of Naturally-Occurring Humoral Immunity to AAV in Sheep

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Gene Therapy Using Nanocarriers for Pancreatic Ductal Adenocarcinoma: Applications and Challenges in Cancer Therapeutics

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Chemogenetic Silencing of NaV1.8-Positive Sensory Neurons Reverses Chronic Neuropathic and Bone Cancer Pain in FLEx PSAM4-GlyR Mice

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AAV Vectored Immunoprophylaxis for Filovirus Infections

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Low Seroprevalence of Neutralizing Antibodies Targeting Two Clade F AAV in Humans

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Preexisting Neutralizing Antibodies to Adeno-Associated Virus Capsids in Large Animals Other Than Monkeys May Confound In Vivo Gene Therapy Studies

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Multiplexing AAV Serotype-Specific Neutralizing Antibodies in Preclinical Animal Models and Humans

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Adeno-Associated Virus Neutralizing Antibodies in Large Animals and Their Impact on Brain Intraparenchymal Gene Transfer

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Preexisting Neutralizing Antibodies against Different Adeno-Associated Virus Serotypes in Humans and Large Animal Models for Gene Therapy

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