Enhanced Expression of Transgenes from Adeno-Associated Virus Vectors with the Woodchuck Hepatitis Virus Posttranscriptional Regulatory Element: Implications for Gene Therapy

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Thy1 transgenic mice expressing the red fluorescent calcium indicator jRGECO1a for neuronal population imaging in vivo

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Adenovirus Ubiquitin-Protein Ligase Stimulates Viral Late mRNA NuclearExport

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A lung tropic AAV vector improves survival in a mouse model of surfactant B deficiency

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WPRE-mediated enhancement of gene expression is promoter and cell line specific

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Adeno-associated viral vector-mediated gene transfer of brain-derived neurotrophic factor reverses atrophy of rubrospinal neurons following both acute and chronic spinal cord injury

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Preservation of forelimb function by UPF1 gene therapy in a rat model of TDP-43-induced motor paralysis

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Improving adeno-associated viral (AAV) vector-mediated transgene expression in retinal ganglion cells: comparison of five promoters

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Optimal Design of a Single Recombinant Adeno-associated Virus Derived from Serotypes 1 and 2 to Achieve More Tightly Regulated Transgene Expression from Nonhuman Primate Muscle

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Long-term Amelioration of Feline Mucopolysaccharidosis VI After AAV-mediated Liver Gene Transfer

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The L444P Gba1 mutation enhances alpha-synuclein induced loss of nigral dopaminergic neurons in mice

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Adeno-associated viral vectors as agents for gene delivery: application in disorders and trauma of the central nervous system

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Schwann cell targeting via intrasciatic injection of AAV8 as gene therapy strategy for peripheral nerve regeneration

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Retinal gene delivery by adeno-associated virus (AAV) vectors: Strategies and applications

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Central leptin gene therapy fails to overcome leptin resistance associated with diet-induced obesity

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Helper‐dependent adenoviral gene therapy mediates long‐term correction of the clotting defect in the canine hemophilia A model

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Leptin-Induced Leptin Resistance Reveals Separate Roles for the Anorexic and Thermogenic Responses in Weight Maintenance

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Neuroprotective Drug for Nerve Trauma Revealed Using Artificial Intelligence

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Choroideremia: from genetic and clinical phenotyping to gene therapy and future treatments

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Central leptin gene delivery evokes persistent leptin signal transduction in young and aged-obese rats but physiological responses become attenuated over time in aged-obese rats

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Inclusion of the Woodchuck Hepatitis Virus Posttranscriptional Regulatory Element Enhances AAV2-Driven Transduction of Mouse and Human Retina

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Long-Term Correction of Ornithine Transcarbamylase Deficiency by WPRE-Mediated Overexpression Using a Helper-Dependent Adenovirus

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Functional expression of complement factor I following AAV-mediated gene delivery in the retina of mice and human cells

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Distinct transduction profiles in the CNS via three injection routes of AAV9 and the application to generation of a neurodegenerative mouse model

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Adeno-Associated Virus-Mediated Rhodopsin Replacement Provides Therapeutic Benefit in Mice with a Targeted Disruption of the Rhodopsin Gene

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The substituted aspartate analogue l-β-threo-benzyl-aspartate preferentially inhibits the neuronal excitatory amino acid transporter EAAT3

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Post-transcriptional regulatory element boosts baculovirus-mediated gene expression in vertebrate cells

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Adeno-associated viral vector gene expression in the adult rat spinal cord following remote vector delivery

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Optimization of transgene expression at the posttranscriptional level in neural cells: implications for gene therapy

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Hypothalamic pro-opiomelanocortin gene delivery ameliorates obesity and glucose intolerance in aged rats

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Therapeutic Levels of Factor IX Expression Using a Muscle-Specific Promoter and Adeno-Associated Virus Serotype 1 Vector

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Intravenous administration of an AAV-2 vector for the expression of factor IX in mice and a dog model of hemophilia B

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Rapid Neurofibrillary Tangle Formation after Localized Gene Transfer of Mutated Tau

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Imaging the response of the retina to electrical stimulation with genetically encoded calcium indicators

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Correction of X-CGD patient HSPCs by targeted CYBB cDNA insertion using CRISPR/Cas9 with 53BP1 inhibition for enhanced homology-directed repair

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Promising and delivering gene therapies for vision loss

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Woodchuck post‐transcriptional element induces nuclear export of myotonic dystrophy 3′ untranslated region transcripts

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Designing and optimizing AAV-mediated gene therapy for neurodegenerative diseases: from bench to bedside

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Enhanced Gene Transfer Efficiency in the Murine Striatum and an Orthotopic Glioblastoma Tumor Model, Using AAV-7- and AAV-8-Pseudotyped Vectors

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Woodchuck hepatitis virus post-transcriptional regulation element enhances transgene expression from adenovirus vectors

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Enhancement of Green Fluorescent Protein Expression in Adeno-Associated Virus with the Woodchuck Hepatitis Virus Post-Transcriptional Regulatory Element

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Woodchuck Hepatitis Virus Posttranscriptional Regulatory Element Enhances Expression of Transgenes Delivered by Retroviral Vectors

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Inclusion of the Woodchuck Hepatitis Virus Posttranscriptional Regulatory Element Enhances AAV2-Driven Transduction of Mouse and Human Retina

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