Microvesicle-associated AAV Vector as a Novel Gene Delivery System

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Chapter 5 Generation of High-Titer Pseudotyped Retroviral Vectors with Very Broad Host Range

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A phase I study of aromatic L-amino acid decarboxylase gene therapy for Parkinson’s disease

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Rapid, Simple, and Versatile Manufacturing of Recombinant Adeno-Associated Viral Vectors at Scale

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A secreted luciferase for ex vivo monitoring of in vivo processes

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Heparan Sulfate Proteoglycans Initiate Dengue Virus Infection of Hepatocytes

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Optimization of self-complementary AAV vectors for liver-directed expression results in sustained correction of hemophilia B at low vector dose

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Efficient Serotype-Dependent Release of Functional Vector into the Culture Medium During Adeno-Associated Virus Manufacturing

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The state of the art of adeno-associated virus-based vectors in gene therapy

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Human Tumor-Derived vs Dendritic Cell-Derived Exosomes Have Distinct Biologic Roles and Molecular Profiles

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Characterization of Tissue Tropism Determinants of Adeno-Associated Virus Type 1

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Protein Transfer Into Human Cells by VSV-G-induced Nanovesicles

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Peripheral transvenular delivery of adeno-associated viral vectors to skeletal muscle as a novel therapy for hemophilia B

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Metabolic biotinylation of cell surface receptors for in vivo imaging

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Adeno-associated virus-mediated gene transfer to hair cells and support cells of the murine cochlea

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Expanding the role of 3-O sulfated heparan sulfate in herpes simplex virus type-1 entry

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In Vitro Packaging of Adeno-Associated Virus DNA

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Preventing Growth of Brain Tumors by Creating a Zone of Resistance

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Unique Characteristics of AAV1, 2, and 5 Viral Entry, Intracellular Trafficking, and Nuclear Import Define Transduction Efficiency in HeLa Cells

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Update on Progress and Hurdles in Novel Genetic Therapies for Hemophilia

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Heparin-binding and patterns of virulence for two recombinant strains of Sindbis virus

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Enhanced in Vivo Imaging of Metabolically Biotinylated Cell Surface Reporters

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Extracellular vesicles: biology and emerging therapeutic opportunities

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Standardization of sample collection, isolation and analysis methods in extracellular vesicle research

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Exosomes: biogenesis, biologic function and clinical potential

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New Technologies for Analysis of Extracellular Vesicles

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Development of exosome-encapsulated paclitaxel to overcome MDR in cancer cells

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Vesiclepedia: A Compendium for Extracellular Vesicles with Continuous Community Annotation

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Using exosomes, naturally-equipped nanocarriers, for drug delivery

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Exosomes: Therapy delivery tools and biomarkers of diseases

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Exosomes and microvesicles: extracellular vesicles for genetic information transfer and gene therapy

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Dynamic Biodistribution of Extracellular Vesicles in Vivo Using a Multimodal Imaging Reporter

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A comprehensive overview of exosomes as drug delivery vehicles — Endogenous nanocarriers for targeted cancer therapy

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Emerging role of extracellular vesicles in inflammatory diseases

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Re-Engineering Extracellular Vesicles as Smart Nanoscale Therapeutics

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Exosomes and Exosome-Inspired Vesicles for Targeted Drug Delivery

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Biology and biogenesis of shed microvesicles

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Tumor-derived microvesicles: shedding light on novel microenvironment modulators and prospective cancer biomarkersPreprint

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Therapeutic Applications of Extracellular Vesicles: Clinical Promise and Open Questions

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Biological Functions and Current Advances in Isolation and Detection Strategies for Exosome Nanovesicles

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Exosomes: Mechanisms of Uptake

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Extracellular vesicles: novel promising delivery systems for therapy of brain diseases.

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AAV vectors: The Rubik’s cube of human gene therapy

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Exosomes derived from miR‐375‐overexpressing human adipose mesenchymal stem cells promote bone regeneration

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Genetically Engineered Microvesicles Carrying Suicide mRNA/Protein Inhibit Schwannoma Tumor Growth

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Bioinspired exosome-like therapeutics and delivery nanoplatforms

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Mesenchymal stem cell exosomes: a two-edged sword in cancer therapy

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Rescue of hearing by gene delivery to inner-ear hair cells using exosome-associated AAV

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Extracellular vesicles and intercellular communication within the nervous system

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Impact of lysosome status on extracellular vesicle content and release

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Exosome-mediated delivery of gene vectors for gene therapy

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Extracellular vesicles as modulators of cell-to-cell communication in the healthy and diseased brain

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Placenta-Derived Exosomes and Syncytiotrophoblast Microparticles and their Role in Human Reproduction: Immune Modulation for Pregnancy Success

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Therapeutic and Diagnostic Translation of Extracellular Vesicles in Cardiovascular Diseases

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Heparin blocks transfer of extracellular vesicles between donor and recipient cells

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CRISPR/Cas9 Mediated Disruption of the Swedish APP Allele as a Therapeutic Approach for Early-Onset Alzheimer’s Disease

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Heparin affinity purification of extracellular vesicles

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Viral vectors for therapy of neurologic diseases

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Therapeutic and diagnostic applications of extracellular vesicles

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Exosomal delivery of therapeutic modulators through the blood–brain barrier; promise and pitfalls

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Exosome-associated AAV2 vector mediates robust gene delivery into the murine retina upon intravitreal injection

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Gene Transfer with AAV9-PHP.B Rescues Hearing in a Mouse Model of Usher Syndrome 3A and Transduces Hair Cells in a Non-human Primate

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Naturally enveloped AAV vectors for shielding neutralizing antibodies and robust gene delivery in vivo

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Alternative Methods for Characterization of Extracellular Vesicles

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Diagnostic and Therapeutic Potential of Exosomes in Cancer: The Beginning of a New Tale?

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